• Increase in a Type of Gut Bacteria Linked to More Pain in Patients with Sickle Cell Disease
  • Sickle Cell Patient with Severe Anemia Rapidly Improves with Voxelotor, Case Study Shows
  • Alzheimer’s Treatment Memantine Shows Promise in Treating Sickle Cell Disease
  • Investigational Therapy Altemia Achieves Main Endpoints in Pediatric Sickle Cell Trial
  • World’s Leading Experts Gathering for International Sickle Cell Conference
  • Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’
  • Georgia Universities Join NIH-funded National Study of Bone Marrow Transplant for SCD
  • SCA Therapy Hydroxyurea Doesn’t Boost Malaria Risk in Sub-Saharan Africa, Study Finds
  • Cydan Raises $34M to Advance New Therapies for Sickle Cell, Other Rare Diseases
  • #NORDsummit – Alternatives to Large Placebo Trials, Grant Awards Among Ways FDA Supporting Rare Diseases, Chief Says
  • Stanford Prof Awarded $5.2M Grant to Advance Gene Therapy Trial for Sickle Cell Disease
  • #NORDsummit – Despite Criticism, Orphan Drug Act Is Working to Advance Needed Treatments, FDA Says