• Patients, Family and Friends to Take Part in Variety of Rare Disease Day Events Worldwide
  • ATS Releases Guidelines for Home Oxygen Therapy in Children with Sickle Cell Disease
  • Emmaus Unveils Co-payment Assistance Program for SCD Endari Patients
  • FDA Revising ‘Draft Guidance’ on Developing Treatments for Rare Diseases
  • Kids with Sickle Cell Anemia are More Sedentary than Healthy Peers, Study Suggests
  • Registration Open for Sickle Cell Foundation of Georgia’s Annual Camp New Hope
  • Vaso-Occlusive Pain Linked to Menstruation in Some Patients, Study Finds
  • Safety and Early Hints of Benefit Seen in Phase 1b Trial of PF-04447943
  • Howard University President Launches ‘Run To Cure Sickle Cell’ Campaign
  • Randomized Trials Needed to Assess Benefits of Salmonella Vaccines in SCD Patients, Study Says
  • Crizanlizumab Designated FDA Breakthrough Therapy for Potential in Vaso-occlusive Crisis Prevention
  • CTX001 Earns FDA’s Fast Track Status for Treating Sickle Cell Disease