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  • Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe
  • Video Games Connect Chronically Ill Children Isolated at Home, Hospital
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  • Partnership to Ensure Supply of LentiGlobin, Potential Gene Therapy
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  • Unity and EU-wide Efforts Focus of Online Rare Disease Meeting
  • Sickle Cell Disease Association, Hemanext Join to Support Programs
  • Unity and EU-wide Efforts Focus of Online Rare Disease Meeting
  • Agios to Decide Next Steps for Mitapivat as SCD Treatment by Mid-year