An advisory committee of the Sickle Cell Disease Association of America is recommending that people with sickle cell disease…
Articles by Joana Carvalho, PhD
APCER Life Sciences has released a report confirming the safety profile of Endari (L-glutamine),…
Fera Pharmaceuticals submitted an application to the U.S. Food and Drug Administration (FDA) requesting orphan drug…
People with sickle cell disease (SCD) treated with hydroxyurea in the U.S. still face many challenges, including the…
FDA-approved therapies for sickle cell disease (SCD) may not be cost-effective at their current prices, according to a…
A potential gene therapy for sickle cell disease (SCD) and beta-thalassemia, known as ARU-1801, has been named…
FT-4202, FORMA Therapeutics’ experimental disease-modifying therapy for sickle cell disease (SCD), shows a favorable safety and pharmacokinetic…
The U.S. Food and Drug Administration (FDA) granted rare pediatric disease designation to ARU-1801, Aruvant’s experimental…
Global Blood Therapeutics (GBT) and Syros Pharmaceuticals have teamed up to discover, develop, and market new therapies for…
Sickle Cell Disease News brought you daily coverage of important discoveries, treatment developments, clinical trials, and other key events…