Patient enrollment has been completed for the Phase 3 RISE UP study, a clinical trial that’s assessing the safety and…
Articles by Marisa Wexler, MS
In the years after undergoing a stem cell transplant, people with sickle cell disease (SCD) exhibit quality-of-life scores…
Children with sickle cell disease (SCD) may be more likely than their peers to have attention-deficit hyperactivity disorder (ADHD),…
Enrollment has been completed in the adolescent group of the Phase 1/2/3 RUBY clinical trial testing Editas Medicine’s gene-editing…
A bone marrow transplant may help reverse heart damage in people with sickle cell disease (SCD), according to a…
A novel small molecule called SR-18292, which acts to boost the production of fetal hemoglobin, was shown to reduce disease…
Women with sickle cell disease who undergo a stem cell transplant can become pregnant and give birth to healthy children,…
TALEN, a gene-editing technology being used by the clinical-stage biopharmaceutical company Cellectis to develop potentially life-changing therapies, was able…
Treatment with the gene-editing therapy Casgevy (exagamglogene autotemcel) substantially decreased the rates of painful vaso-occlusive crises (VOCs) among…
England’s National Institute for Health and Care Excellence (NICE) has published final draft guidance recommending the country’s National Health Service…