The SECURE-SCD registry, which is collecting de-identified data on individuals with sickle cell disease (SCD) who develop…
Articles by Marisa Wexler, MS
A European Medicines Agency (EMA) committee has adopted a positive opinion on Novartis‘s Adakveo (crizanlizumab) for the…
Blood stem cell transplant from unrelated donors is a feasible strategy in people with sickle cell disease (SCD), with…
FT-4202 — an investigational treatment for sickle cell disease (SCD) — has a favorable safety profile and the expected…
Global Blood Therapeutics (GBT) plans to submit a marketing authorization application to the European Medicines Agency (EMA)…
Global Blood Therapeutics (GBT) will ask the U.S. Food and Drug Administration (FDA) to allow children with sickle cell disease (SCD),…
The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to Forma Therapeutics‘ FT-4202 for the…
Children and adolescents with sickle cell disease (SCD) who lack vitamin D are hospitalized more often due to…
The American Society of Hematology released new clinical guidelines on the use of blood transfusions in people with…
Voxelotor can reduce the severity of existing leg ulcers and the incidence of new ones in people with sickle cell…