• ‘Rare Impact Awards’ Dinner Marks Orphan Drug Act and NORD at 35
  • FDA Accepts Collaborative IND Application for BIVV003 to Treat Sickle Cell Disease
  • Stigmatizing Language in Medical Records Affects Patient Care, Study Shows
  • St. Jude Hospital Given $1M Grant from Links Foundation to Advance 3 Sickle Cell Disease Programs
  • Stem Cells from Half-Matched Donors in New Approach Reported to Cure 7 Sickle Cell Patients
  • #ECRD2018 – Patient Access and Collaboration Focus of Eurordis Meeting May 10-12
  • Sickle Cell Groups, Pfizer Work to Bring African-Americans into Clinical Trials
  • Human Genome Project Team at NIH Honored for Advancing Research into Genetic Diseases
  • In-person Caregiver Education Increases Sickle Cell Trait Knowledge, Study Reports
  • Sickle Cell Disease Researchers Identify a Children’s Stroke Prediction Tool
  • Novo Nordisk Obtains Worldwide Rights to EpiDestiny’s Sickle Cell Disease Therapy