BEAM-101, a one-time, gene-edited cell therapy, continues to show durable therapeutic benefits more than one year after treatment in people with sickle cell disease (SCD), according to new data from the Phase 1/2 BEACON trial. The treatment’s developer, Beam Therapeutics, shared data from the first 17 patients dosed…
Read more
I’m writing from the heart of the EHA2025 Congress, hosted by the European Hematology Association (EHA), in Milan, Italy. I’m surrounded by leading experts, researchers, and, most importantly, fellow patients who understand what it’s like to live with sickle cell disease. Conferences like this aren’t just for clinicians…
From illuminating public buildings in red to candlelight vigils and walks, supporters are gearing up to raise awareness and increase public knowledge about sickle cell disease (SCD) on June 19, World Sickle Cell Day. This year’s global theme is “Global Action, Local Impact: Empowering Communities for Effective Self-Advocacy.” SCD…
In honor of World Sickle Cell Day, held June 19, I would like to highlight some incredible U.K.-based organizations I’ve had the pleasure of working with recently. These groups are not only changing the narrative of what it means to live with sickle cell disease, but they’re also challenging…
Becoming educated and informed about sickle cell disease is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your sickle cell disease journey.
A stem cell transplant is the only potential cure for sickle cell disease, but there are a variety of other treatment approaches. Here you can find more information about current treatments as well as experimental therapies in the pipeline.
Get regular updates to your inbox.
