Brothers Cameron, Cayden, and Carmani Boozer have partnered with NMDP to encourage more young adults to join its blood stem cell donor registry and help people with sickle cell disease (SCD), blood cancers, and other serious blood disorders access potentially curative transplants. NMDP, formerly known as the National…
Discussion
I wasn’t supposed to be writing my next column yet. In fact, I specifically requested that this piece be published on June 19, World Sickle Cell Day. For me, the day is more than an awareness campaign. It is a time to celebrate the resilience, strength, and courage of millions…
Discussion
Agios Pharmaceuticals’ medication mitapivat rapidly increased levels of the oxygen-carrying protein hemoglobin in patients ages 16 and older with sickle cell disease (SCD), while also being linked to a lower blood transfusion burden over 52 weeks. These are new data from the Phase 3 portion of the global…
Discussion
The U.S. Food and Drug Administration is reviewing an application from Vertex Pharmaceuticals seeking approval of Casgevy (exagamglogene autotemcel) for children with sickle cell disease (SCD) as young as 5 years old. The gene-editing therapy is currently approved in the U.S. and elsewhere for people ages 12 and older with…
Becoming educated and informed about sickle cell disease is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your sickle cell disease journey.
A stem cell transplant is the only potential cure for sickle cell disease, but there are a variety of other treatment approaches. Here you can find more information about current treatments as well as experimental therapies in the pipeline.
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