The U.S. Food and Drug Administration (FDA) has extended the review period for mitapivat as a potential treatment for sickle cell disease (SCD), with a decision now expected by Feb. 1, 2027. The delay follows the FDA’s request for additional information to determine whether a Risk Evaluation and…
Discussion
One of the most challenging things about living with sickle cell disease is that, despite the planning, preparation, and precautions we patients take, a crisis or a pain episode can still unexpectedly happen. Sometimes, even when we do everything right to look after ourselves, our bodies remind us that…
Discussion
I tell my children that we are a family that makes really good lemonade. Meaning, when life gives us something difficult or sour, we have an uncanny ability to turn it into something positive or sweet. I believe that is mostly due to the skills we have acquired while battling…
Discussion
Recently, I’ve been receiving international professional opportunities, which have made me think about a question I’ve avoided for years: What would I do if an opportunity I’ve always dreamed about required me to travel abroad by airplane? What happens when one of your greatest career dreams comes within reach, but…
Becoming educated and informed about sickle cell disease is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your sickle cell disease journey.
A stem cell transplant is the only potential cure for sickle cell disease, but there are a variety of other treatment approaches. Here you can find more information about current treatments as well as experimental therapies in the pipeline.
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