A high dose of pociredir, Fulcrum Therapeutics’ oral drug candidate for sickle cell disease (SCD), boosted fetal hemoglobin (HbF) levels and reduced red blood cell destruction — thereby easing symptoms of anemia — in a small group of patients with the blood disorder. These are the latest results…
Most women and girls with sickle cell disease (SCD) experience disease-related pain during menstrual periods, but many are unaware that medical treatments — such as birth control pills — may help alleviate period-related pain in SCD, according to a new study by U.S. researchers. Based on these findings, the…
As they shift from pediatric to adult care, young adults with sickle cell disease (SCD) appear to visit the emergency room more often and be prescribed less hydroxyurea, a preventive treatment approved to reduce the frequency of painful crises, according to a study in the U.S. Data also…
A small clinical trial testing Agios Pharmaceuticals’ oral therapy candidate tebapivat against a placebo for easing symptoms in people with sickle cell disease (SCD) has completed enrollment, the company announced. Agios expects to report early results from the Phase 2 trial later this year, according to a…
Becoming educated and informed about sickle cell disease is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your sickle cell disease journey.
A stem cell transplant is the only potential cure for sickle cell disease, but there are a variety of other treatment approaches. Here you can find more information about current treatments as well as experimental therapies in the pipeline.
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