ReachBio Launches Screening Platform to Find New Therapies for SCD
ReachBio Research Labs has created a drug screening platform to discover therapeutic compounds that trigger the production of fetal hemoglobin (HbF) to treat ... Read more
Updates
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ICER Will Compare Lead Candidate Therapies Crizanlizumab and Voxelotor for Efficacy, Value
An upcoming analysis by the Institute for Clinical and Economic Review (ICER) will compare the clinical efficacy and economic value of Novartis’ crizanlizumab ... Read more -
New Technology May Allow for Better Monitoring of Sickle Cell Disease
A new way to monitor blood cells that doesn’t require microscopic imaging or biochemical markers may allow for better management of sickle cell ... Read more -
Cognitive Decline Not Evident in Black Americans with Sickle Cell Trait, Study Finds
African-Americans with sickle cell trait, carriers for sickle cell but without the disease, have no greater risk of cognitive decline than other adults of ... Read more
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Survival After Kidney Transplant Lower in SCD Patients Than Other Kidney Disease Patients, Analysis Shows
Survival of sickle cell disease patients (SCD) with end-stage renal disease who undergo kidney ... -
Phase 3 Trial of Rivipansel in Treating SCD Pain Crisis Fails to Meet Goals, Pfizer Announces
The Phase 3 RESET trial testing the effectiveness and safety of rivipansel (GMI-1070), Pfizer‘s investigational candidate ... -
Rare Disease Groups Seek Public Support to Renew Newborn Screening Act in Senate
Screening newborns for genetic diseases with treatments that can prevent crippling or deadly progression, ... -
Oklahoma Ranks Lowest on Programs Key to Rare Diseases on NORD’s 2019 State Report Card
Oklahoma suffers more tornadoes than any other state, has the highest per-capita rate of ... -
NHLBI Stepping Up Efforts to Apprise SCD Patients of Therapies and Trials
Wide interest in a CBS 60 Minutes story about a Florida woman with sickle ... -
Emmaus Takes ‘Sideline Sickle Cell’ Campaign to Annual SCD Family and Educational Event
Emmaus Life Sciences, accompanied by the Emmy Award-winning National Football League (NFL) broadcaster Solomon ...
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Kids with Sickle Cell Disease at Risk for Lead Poisoning, NYC Study Shows
News
National and local policies have led to large reductions in lead poisoning cases overall in the U.S., but severe cases are still common among children. Recently, researchers at the New York City Department of Health and Mental Hygiene (DOHMH) investigated sources of exposure, risk factors, and ... Read more